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Gene Therapy & Genomic Medicine
CRISPR edits, delivery vectors, rare‑disease trials, and approvals.
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Latest in Gene Therapy & Genomic Medicine
Skeletal editing can transform molecules’ biological activity
2+ hour, 48+ min ago (238+ words) Federation: Log in through a federation service that connects your organization to multiple systems. Use this option if your organization instructs you to use federated sign-in. Oxygen-to-nitrogen swap changes a natural product’s mechanism of action Researchers in Korea have used…...
Custom genetic codes can now be created with ease
3+ hour, 31+ min ago (425+ words) Federation: Log in through a federation service that connects your organization to multiple systems. Use this option if your organization instructs you to use federated sign-in. Custom genetic codes can now be created with ease Nearly every organism on the…...
SANA: IND and phase I/II trial for diabetes therapy and first-in-human CAR T data expected within 12 months
4+ hour, 59+ min ago (94+ words) TradingView SANA: IND and phase I/II trial for diabetes therapy and first-in-human CAR T data expected within 12 months Two innovative platforms are advancing: a hypoimmune cell therapy for type 1 diabetes, with an IND and phase I/II trial planned…...
CRISPR-Combo Speeds Gene-Edited Crop Regeneration
8+ hour, 15+ min ago (506+ words) Editing a plant’s genes is only one step in developing an improved crop. Scientists must also regenerate a complete plant from a small number of edited cells — a process that can be slow, unreliable or impossible in some species. Researchers…...
Cracking cell dynamics with single-cell proteomics and CRISPR
4+ day, 8+ hour ago (425+ words) Sponsored by Cell Signaling Technology and Myllia Join this virtual panel to explore how combining pooled CRISPR screening with intracellular protein detection can reveal cellular responses and signalling dynamics that transcriptomics alone may miss. Single-cell transcriptomics can show which genes…...
Cellectis scraps CAR-T pipeline in gene editing pivot - European Biotechnology Magazine
13+ hour, 53+ min ago (424+ words) French biotech Cellectis is abandoning development of its two internal allogeneic CAR-T programs and repositioning itself as an in vivo gene editing company focused initially on cardiovascular disease. Why it matters: The move is a dramatic reset for one of…...
YPrime Guide: Supply Management Critical to IRT Trial Success for Biotech Sponsors
14+ hour, 45+ min ago (366+ words) clinicaltrialvanguard.com YPrime Guide: Supply Management Critical to IRT Trial Success for Biotech Sponsors Supply management, not randomization, is where IRT systems win or lose a trial budget. That framing sits at the center of a new operational guide from…...
New gene therapy treats liver disorder in growing children
16+ hour, 1+ min ago (369+ words) Researchers at the Children’s Medical Research Institute (CMRI), led by Associate Professor Samantha Ginn, have taken a step towards solving one of the biggest challenges in gene therapy for children with metabolic liver disorders: growth itself. Conventional gene therapy for…...
Blood centers can help biopharma scale cell and gene therapies
17+ hour, 6+ min ago (661+ words) CAR T cell therapies are growing their foothold beyond cancer and into autoimmune indications. Gene editing therapies, meanwhile, offer one-and-done treatments for sickle cell disease and have proven value in rarer diseases as well. But as cell and gene therapy…...
Transgenerational repairs of chromosomes
18+ hour, 34+ min ago (23+ words) (IMAGE) EurekAlert! Transgenerational repairs of chromosomes More on this News Release Chromosome repair passed down from generation to generation...